I’ve been home for 30 minutes, and I have cried 3 times. Nice.
Oh for my non-facebook friends…. FDA nixed the exon-skipping drug. Said it was premature and that they needed a new study.
Fuck them. They have an accelerated program for diseases JUST LIKE DUCHENNE!!!!!!!!!!!!!!!! So what the fuck is so hard that they can’t see it fits in the same category??
…………Determining whether a condition is serious is a matter of judgment, but generally is based on whether the drug will have an impact on such factors as survival, day-to-day functioning, or the likelihood that the condition, if left untreated, will progress from a less severe condition to a more serious one.